3
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| developmental and epileptic encephalopathy | relutrigineSmall molecule, non-isoform selective NaV persistent current inhibitorSCN2A mRNA knockdown antisense oligonucleotide | Orphan Designation | - |
| developmental and epileptic encephalopathy, 11 | relutrigineSmall molecule, non-isoform selective NaV persistent current inhibitorSCN2A mRNA knockdown antisense oligonucleotide | Orphan Designation | - |
| developmental and epileptic encephalopathy, 13 | relutrigineSmall molecule, non-isoform selective NaV persistent current inhibitorSCN2A mRNA knockdown antisense oligonucleotide | Orphan Designation | - |
| developmental and epileptic encephalopathy, 62 | relutrigineSCN2A mRNA knockdown antisense oligonucleotide | Orphan Designation | - |
| developmental and epileptic encephalopathy, 6A | relutrigineSCN2A mRNA knockdown antisense oligonucleotide | Orphan Designation | - |
| undetermined early-onset epileptic encephalopathy | relutrigineSmall molecule, non-isoform selective NaV persistent current inhibitorSCN2A mRNA knockdown antisense oligonucleotide | Orphan Designation | - |