2
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Allan-Herndon-Dudley syndrome | Tetrabenazine | Orphan Designation | - |
| Huntington disease | Xenazine | Orphan Designation | - |
| Pitt-Hopkins syndrome | Tetrabenazine | Orphan Designation | - |
| chorea gravidarum | Xenazine | Orphan Designation | - |
| chorea, benign familial | Xenazine | Orphan Designation | - |
| chorea-acanthocytosis | Xenazine | Orphan Designation | - |
| intellectual disability, autosomal recessive 42 | Tetrabenazine | Orphan Designation | - |