5
Orphan Designations
1
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Acanthamoeba keratitis | miltefosine | Orphan Designation | - |
| disseminated | miltefosine | Orphan Designation | - |
| disseminated peritoneal leiomyomatosis | miltefosine | Orphan Designation | - |
| disseminated superficial actinic porokeratosis | miltefosine | Orphan Designation | - |
| granulomatous amebic encephalitis | miltefosine | Orphan Designation | - |
| granulomatous disease, chronic, X-linked | miltefosine | Orphan Designation | - |
| granulomatous disease, chronic, autosomal recessive, 5 | miltefosine | Orphan Designation | - |
| primary amebic meningoencephalitis | miltefosine | Orphan Designation | - |
| primary biliary cholangitis | miltefosine | Orphan Designation | - |
| primary cutaneous lymphoma | miltefosine | Orphan Designation | - |
| schistosomiasis | miltefosine | Orphan Designation | - |