3
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Crigler-Najjar syndrome | heterologous human liver derived progenitor cells | Orphan Designation | - |
| urea cycle disorder | heterologous human adult liver derived progenitor cells (HHALPC)human heterologous liver cells | Orphan Designation | - |