1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Bicervical bicornuate uterus with patent cervix and vagina | Ryplazim | Orphan Designation | - |
| Char syndrome | Ryplazim | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | Ryplazim | Orphan Designation | - |
| hypoplasminogenemia | Ryplazim | Orphan Designation | - |
| multisystemic smooth muscle dysfunction syndrome | Ryplazim | Orphan Designation | - |
| natal teeth-intestinal pseudoobstruction-patent ductus syndrome | Ryplazim | Orphan Designation | - |