1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Behr syndrome | Autologous incubated macrophage | Orphan Designation | - |
| PCWH syndrome | Autologous incubated macrophage | Orphan Designation | - |
| chorea-acanthocytosis | Autologous incubated macrophage | Orphan Designation | - |
| glucocorticoid therapy, response to | Autologous incubated macrophage | Orphan Designation | - |
| major depressive disorder | Autologous incubated macrophage | Orphan Designation | - |
| vitamin K-antagonist embryofetopathy | Autologous incubated macrophage | Orphan Designation | - |