1
Orphan Designations
1
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Kohlschutter-Tonz syndrome-like | Tzield | Orphan Designation | - |
| RECON progeroid syndrome | Tzield | Orphan Designation | - |
| erythrokeratodermia variabilis | Tzield | Orphan Designation | - |
| erythrokeratodermia variabilis et progressiva 1 | Tzield | Orphan Designation | - |
| nodular basal cell carcinoma | Tzield | Orphan Designation | - |
| peroxisome biogenesis disorder 5A (Zellweger) | Tzield | Orphan Designation | - |