1
Orphan Designations
0
FDA Approvals
10
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| adult neuronal ceroid lipofuscinosis | ProvayBlue | Orphan Designation | - |
| adult pleomorphic rhabdomyosarcoma | ProvayBlue | Orphan Designation | - |
| adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia | ProvayBlue | Orphan Designation | - |
| adult-onset proximal spinal muscular atrophy, autosomal dominant | ProvayBlue | Orphan Designation | - |
| drug-induced methemoglobinemia | ProvayBlue | Orphan Designation | - |
| inherited | ProvayBlue | Orphan Designation | - |
| pediatric hepatocellular carcinoma | ProvayBlue | Orphan Designation | - |
| pediatric ovarian dysgerminoma | ProvayBlue | Orphan Designation | - |
| pediatric-onset Graves disease | ProvayBlue | Orphan Designation | - |
| primary adult heart tumor | ProvayBlue | Orphan Designation | - |