2
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| developmental and epileptic encephalopathy, 1 | Vigafyde | Orphan Designation | - |
| developmental and epileptic encephalopathy, 2 | Vigafyde | Orphan Designation | - |
| developmental and epileptic encephalopathy, 27 | Vigafyde | Orphan Designation | - |
| developmental and epileptic encephalopathy, 43 | Vigafyde | Orphan Designation | - |
| developmental and epileptic encephalopathy, 44 | Vigafyde | Orphan Designation | - |
| infantile spasms | Vigafyde | Orphan Designation | - |
| tuberous sclerosis | vigabatrin | Orphan Designation | - |