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Ra Pharmaceuticals, Inc. — Rare Disease Pipeline | Kisho

Ra Pharmaceuticals, Inc.

Other

Orphan Designations

0 approved

FDA Approvals

Active Trials

Rare Diseases

across 6 areas

News (30d)

Quiet

Ra Pharmaceuticals, Inc. is a company with 1 orphan drug designation across 3 rare diseases.

Diversified Portfolio

Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.

Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA

Approved: 0

In Trials: 0

Designated Only: 3

3 total diseases

Disease	Drug(s)	Stage
paroxysmal nocturnal hemoglobinuria	Synthetic 15-amino-acid macrocyclic peptide acylated with a ethyleneglycol palmitoylated linker	Des.TrialAppr.
paroxysmal nocturnal hemoglobinuria 1	Synthetic 15-amino-acid macrocyclic peptide acylated with a ethyleneglycol palmitoylated linker	Des.TrialAppr.
paroxysmal nocturnal hemoglobinuria 2	Synthetic 15-amino-acid macrocyclic peptide acylated with a ethyleneglycol palmitoylated linker	Des.TrialAppr.