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Rare Partners srl Impresa Sociale — Rare Disease Pipeline | Kisho | Kisho
Rare Partners srl Impresa Sociale
Other
2
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
Pipeline
Designations
News
Diseases
Disease
Drug(s)
Designation
Approved
beta-thalassemia HBB/LCRB
sirolimus
Orphan Designation
-
sickle cell disease
sirolimus
Orphan Designation
-
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