2
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute flaccid myelitis | pegtarazimod | Orphan Designation | - |
| acute graft versus host disease | pegtarazimod | Orphan Designation | - |
| acute lymphoblastic leukemia | pegtarazimod | Orphan Designation | - |
| idiopathic neonatal atrial flutter | Peptide Inhibitor of Complement C1 | Orphan Designation | - |
| neonatal antiphospholipid syndrome | Peptide Inhibitor of Complement C1 | Orphan Designation | - |
| perinatal asphyxia | Peptide Inhibitor of Complement C1 | Orphan Designation | - |