4
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Diamond-Blackfan anemia 1 | Anagrelide | Orphan Designation | - |
| acquired polycythemia vera | Anagrelide | Orphan Designation | - |
| argininosuccinic aciduria | Anagrelide | Orphan Designation | - |
| central precocious puberty | Supprelin InjectionDeslorelin | Orphan Designation | - |
| idiopathic hypereosinophilic syndrome | Anagrelide | Orphan Designation | - |