1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Baraitser-Winter syndrome 1 | picibanil | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | picibanil | Orphan Designation | - |
| natal teeth-intestinal pseudoobstruction-patent ductus syndrome | picibanil | Orphan Designation | - |