2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Huntington disease | (3beta,24S)-25,25,25-trifluoro-3-methyl-26,27-dinorergost-5-ene-3,24-diol | Orphan Designation | - |
| Huntington disease-like 1 | (3beta,24S)-25,25,25-trifluoro-3-methyl-26,27-dinorergost-5-ene-3,24-diol | Orphan Designation | - |
| Huntington disease-like 2 | (3beta,24S)-25,25,25-trifluoro-3-methyl-26,27-dinorergost-5-ene-3,24-diol | Orphan Designation | - |
| new-onset refractory status epilepticus | allopregnanolone | Orphan Designation | - |