2
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Becker muscular dystrophy | Oxandrolone | Orphan Designation | - |
| Char syndrome | Oxandrolone | Orphan Designation | - |
| amyloidosis bronchopulmonary | Recombinant human superoxide dismutase | Orphan Designation | - |
| bronchopulmonary dysplasia | Recombinant human superoxide dismutase | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | Oxandrolone | Orphan Designation | - |
| mucopolysaccharidosis-plus syndrome | Recombinant human superoxide dismutase | Orphan Designation | - |
| multisystemic smooth muscle dysfunction syndrome | Oxandrolone | Orphan Designation | - |
| natal teeth-intestinal pseudoobstruction-patent ductus syndrome | Oxandrolone | Orphan Designation | - |