1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Alstrom syndrome | Alprostadil | Orphan Designation | - |
| Ogden syndrome | Alprostadil | Orphan Designation | - |
| spinal muscular atrophy with congenital bone fractures 1 | Alprostadil | Orphan Designation | - |