6
Orphan Designations
0
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| 22q11.2 deletion syndrome | Thymalfasin | Orphan Designation | - |
| Alstrom syndrome | thymalfasin | Orphan Designation | - |
| COG8-congenital disorder of glycosylation | thymalfasin | Orphan Designation | - |
| DiGeorge syndrome | Thymalfasin | Orphan Designation | - |
| Hodgkins lymphoma | Thymalfasin | Orphan Designation | - |
| Sjogren syndrome | thymalfasin | Orphan Designation | - |
| cystic fibrosis | 8 Cyclopentyl 1,3-dipropylxanthine | Orphan Designation | - |
| hepatocellular carcinoma | Thymalfasin | Orphan Designation | - |
| malignant pancreatic neoplasm | Brivudin | Orphan Designation | - |
| stage II endometrioid carcinoma | Thymalfasin | Orphan Designation | - |
| stage IVb bladder cancer | Thymalfasin | Orphan Designation | - |