5
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| T-cell non-Hodgkin lymphoma | 4-[[[4-[5-chloro-2-[[trans-4-[[(1R)-2-methoxy-1-methyl ethyl] amino] cyclohexyl] amino] -4-pyridinyl]-2-thiazolyl] amino] methyl] tetrahydro-2H-pyran-4-carbonitrile dimaleate | Orphan Designation | - |
| acute myeloid leukemia | 4-[[[4-[5-chloro-2-[[trans-4-[[(1R)-2-methoxy-1-methyl ethyl] amino] cyclohexyl] amino] -4-pyridinyl]-2-thiazolyl] amino] methyl] tetrahydro-2H-pyran-4-carbonitrile dimaleateHuman Wilms tumor protein 1 peptides | Orphan Designation | - |
| mesothelioma | Human wilms tumor protein 1 peptides | Orphan Designation | - |
| plasma cell myeloma | galinpepimut-S | Orphan Designation | - |