1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| autosomal dominant cerebellar ataxia, deafness and narcolepsy | Gamma-hydroxybutyric acid | Orphan Designation | - |
| narcolepsy | Gamma-hydroxybutyric acid | Orphan Designation | - |
| narcolepsy-cataplexy syndrome | Gamma-hydroxybutyric acid | Orphan Designation | - |