3
Orphan Designations
0
FDA Approvals
10
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Dubowitz syndrome | Xatmep | Orphan Designation | - |
| glioma susceptibility 3 | Xatmep | Orphan Designation | - |
| hypertensive disorder | enalapril maleate (powder for oral solution) | Orphan Designation | - |
| pediatric hepatocellular carcinoma | Xatmep | Orphan Designation | - |
| pediatric ovarian dysgerminoma | Xatmep | Orphan Designation | - |
| pediatric-onset Graves disease | Xatmep | Orphan Designation | - |
| pulmonary hypertension, neonatal | lisinopril oral solution | Orphan Designation | - |
| pulmonary hypertension, primary, 2 | lisinopril oral solution | Orphan Designation | - |
| pulmonary hypertension, primary, 3 | lisinopril oral solution | Orphan Designation | - |
| thrombocytopenia 5 | Xatmep | Orphan Designation | - |