3
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| cholangiocarcinoma | cotsiranib | Orphan Designation | - |
| hepatocellular carcinoma | small interfering RNA targeting TGF-Beta1 and COX-2 mRNA | Orphan Designation | - |
| intrahepatic cholangiocarcinoma | cotsiranib | Orphan Designation | - |
| primary sclerosing cholangitis | Cotsiranib | Orphan Designation | - |
| sarcomatous intrahepatic cholangiocarcinoma | cotsiranib | Orphan Designation | - |