2
Orphan Designations
1
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| ACTH-independent macronodular adrenal hyperplasia 2 | Vykat XR | Orphan Designation | - |
| Prader-Willi syndrome | Vykat XR | Orphan Designation | - |
| glycogen storage disease IX | Diazoxide Choline | Orphan Designation | - |
| glycogen storage disease IXc | Diazoxide Choline | Orphan Designation | - |
| glycogen storage disease Ib | Diazoxide Choline | Orphan Designation | - |
| hyperinsulinemic hypoglycemia, familial, 1 | Vykat XR | Orphan Designation | - |
| hyperinsulinemic hypoglycemia, familial, 2 | Vykat XR | Orphan Designation | - |