1
Orphan Designations
0
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Chiari malformation type I | Myobloc | Orphan Designation | - |
| aneurysm-osteoarthritis syndrome | Myobloc | Orphan Designation | - |
| angiostrongyliasis | Myobloc | Orphan Designation | - |
| cardiac valvular defect, developmental | Myobloc | Orphan Designation | - |
| cervical dystonia | Myobloc | Orphan Designation | - |
| hereditary spastic paraplegia 25 | Myobloc | Orphan Designation | - |
| multiple congenital anomalies-hypotonia-seizures syndrome 2 | Myobloc | Orphan Designation | - |
| neurodevelopmental disorder with coarse facies and mild distal skeletal abnormalities | Myobloc | Orphan Designation | - |
| neurodevelopmental disorder with seizures, microcephaly, and brain abnormalities | Myobloc | Orphan Designation | - |