1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| intractable diarrhea-choanal atresia-eye anomalies syndrome | resiniferatoxin | Orphan Designation | - |
| myoclonus, intractable, neonatal | resiniferatoxin | Orphan Designation | - |
| refractory celiac disease | resiniferatoxin | Orphan Designation | - |