1
Orphan Designations
0
FDA Approvals
1
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| pulmonary non-tuberculous mycobacterial infection | Sodium (R)-2-(5-(2-(3-ethylureido)-5-fluoro-4-(tetrahydrofuran-2-yl)-1H-benzo[d]imidazole-6-yl)pyrimidin-2-yl)propan-2-yl hydrogen phosphate | Orphan Designation | - |