1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute flaccid myelitis | universal CAR-T cell injection targeting NKG2D ligands/OX40/CD70/BCMA | Orphan Designation | - |
| acute graft versus host disease | universal CAR-T cell injection targeting NKG2D ligands/OX40/CD70/BCMA | Orphan Designation | - |
| acute lymphoblastic leukemia | universal CAR-T cell injection targeting NKG2D ligands/OX40/CD70/BCMA | Orphan Designation | - |