1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| amyloidosis bronchopulmonary | Mesenchymal Stem Cell-derived Extracellular Vesicles | Orphan Designation | - |
| bronchopulmonary dysplasia | Mesenchymal Stem Cell-derived Extracellular Vesicles | Orphan Designation | - |
| mucopolysaccharidosis-plus syndrome | Mesenchymal Stem Cell-derived Extracellular Vesicles | Orphan Designation | - |