2
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Cushing syndrome | fluasterone | Orphan Designation | - |
| NAFLD1 | fluasterone | Orphan Designation | - |
| ectopic Cushing syndrome | fluasterone | Orphan Designation | - |
| endogenous Cushing syndrome | fluasterone | Orphan Designation | - |
| metabolic dysfunction-associated steatohepatitis | fluasterone | Orphan Designation | - |
| primary sclerosing cholangitis | Gly-Trp-Thr-Leu-Asn-Ser-Ala-Gly-Tyr-Leu-Leu- Gly-Pro-Pro-Pro-Ala-Leu-Ala-Leu-Ala-NH2 | Orphan Designation | - |