4
Orphan Designations
1
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| B-cell adult acute lymphocytic leukemia | Revuforj | Orphan Designation | - |
| T-cell adult acute lymphocytic leukemia | Revuforj | Orphan Designation | - |
| acute leukemia of ambiguous lineage | Revuforj | Orphan Designation | - |
| acute lymphoblastic leukemia | Revuforj | Orphan Designation | - |
| acute myeloid leukemia | Revuforj | Orphan Designation | - |
| adult acute monocytic leukemia | Revuforj | Orphan Designation | - |
| ataxia, early-onset, with oculomotor apraxia and hypoalbuminemia | Revuforj | Orphan Designation | - |
| cancer-related condition | Revuforj | Orphan Designation | - |
| childhood acute myeloid leukemia | Revuforj | Orphan Designation | - |
| idiopathic pulmonary fibrosis | axatilimab | Orphan Designation | - |
| toxic or drug-related embryofetopathy | Revuforj | Orphan Designation | - |