2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| classic phenylketonuria | a phenylalanine consuming engineered bacteria | Orphan Designation | - |
| homocystinuria | live biotherapeutic consisting of metP and metDC genes which are incorporated into the genome of a probiotic strain of E. coli Nissie 1917 | Orphan Designation | - |
| phenylketonuria | a phenylalanine consuming engineered bacteria | Orphan Designation | - |
| phenylketonuria | a phenylalanine consuming engineered bacteria | Orphan Designation | - |