3
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute myeloid leukemia | tamibarotene | Orphan Designation | - |
| childhood myelodysplastic syndrome | tamibarotene | Orphan Designation | - |
| malignant pancreatic neoplasm | (S)-7-(dimethylphosphoryl)-3-(2-((6,6-dimethylpiperidin-3-yl)amino)-5-(trifluoromethyl)pyrimidin-4-yl)-1H-indole-6-carbonitrile | Orphan Designation | - |
| myelodysplastic syndrome | tamibarotene | Orphan Designation | - |
| myelodysplastic syndrome with excess blasts-2 | tamibarotene | Orphan Designation | - |