1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Leber congenital amaurosis 6 | Troleandomycin | Orphan Designation | - |
| X-linked intellectual disability, Cantagrel type | Troleandomycin | Orphan Designation | - |
| severe Canavan disease | Troleandomycin | Orphan Designation | - |