3
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| STAT3-related early-onset multisystem autoimmune disease | angiotensin 1-7 | Orphan Designation | - |
| autoimmune lymphoproliferative syndrome | angiotensin 1-7 | Orphan Designation | - |
| autosomal recessive osteopetrosis 2 | angiotensin 1-7 | Orphan Designation | - |
| autosomal recessive osteopetrosis 3 | angiotensin 1-7 | Orphan Designation | - |
| autosomal recessive osteopetrosis 5 | angiotensin 1-7 | Orphan Designation | - |
| myelodysplastic syndrome | Angiotensin 1-7 | Orphan Designation | - |
| neutropenia | Angiotensin 1-7 | Orphan Designation | - |
| refractory anemia with excess blasts in transformation | angiotensin 1-7 | Orphan Designation | - |