1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| leukodystrophy, demyelinating, adult-onset, autosomal dominant, typical | autologous neo-uninary conduit | Orphan Designation | - |
| multiple system atrophy | autologous neo-uninary conduit | Orphan Designation | - |
| urinary bladder, atony of | autologous neo-uninary conduit | Orphan Designation | - |