1
Orphan Designations
0 approved, 1 designated
0
FDA Approvals
2
Active Trials
200 recruiting
2
Rare Diseases
across 3 areas
0
News (30d)
Quiet
TESS Research Foundation is a company with 1 orphan drug designation across 2 rare diseases. Active clinical trials in 2 indications. gene therapy candidates in 1 disease. 2 active policy bills affect their portfolio.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| developmental and epileptic encephalopathy, 25 | Adeno-associated virus serotype 9 (AAV9) vector with engineered transgene encoding the human SLC13A5 protein. | Des.TrialAppr. |
| epilepsy | - | Des.TrialAppr. |
100% of portfolio targets high unmet need diseases
0
overlap in 2+ diseases
1/2
candidate diseases
0
avg importance: 0
2
affecting portfolio
100% of portfolio targets high unmet need diseases
0
overlap in 2+ diseases
1/2
candidate diseases
0
avg importance: 0
2
affecting portfolio