1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| complex regional pain syndrome | zoledronate D,L-lysine monohydrate (ZLM) | Orphan Designation | - |
| facioscapulohumeral muscular dystrophy | zoledronate D,L-lysine monohydrate (ZLM) | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 6 (hepatocerebral type) | zoledronate D,L-lysine monohydrate (ZLM) | Orphan Designation | - |