3
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| DYRK1A-related intellectual disability syndrome | Methoxsalen8-methoxsalen | Orphan Designation | - |
| acute intermittent porphyria | methoxsalen | Orphan Designation | - |
| acute stress disorder | methoxsalen | Orphan Designation | - |
| anosmia for isobutyric acid | Methoxsalen8-methoxsalen | Orphan Designation | - |
| neuroacanthocytosis | Methoxsalen8-methoxsalen | Orphan Designation | - |
| yellow fever | methoxsalen | Orphan Designation | - |