2
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Kohlschutter-Tonz syndrome-like | Microvesiculated modified glycosylated tissue factor | Orphan Designation | - |
| Weaver syndrome | Microvesiculated modified glycosylated tissue factor | Orphan Designation | - |
| non-amyloid fibrillary glomerulopathy | Microvesiculated modified glycosylated tissue factor | Orphan Designation | - |