4
Orphan Designations
0 approved, 4 designated
0
FDA Approvals
1
Active Trials
200 recruiting
5
Rare Diseases
across 10 areas
0
News (30d)
Quiet
TopAlliance Biosciences, Inc. is a company with 4 orphan drug designations across 5 rare diseases. Active clinical trials in 1 indication.
Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.
Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA
| Disease | Drug(s) | Stage |
|---|---|---|
| esophageal cancer | Toripalimab | Des.TrialAppr. |
| lymphoma | - | Des.TrialAppr. |
| mucosal melanoma | toripalimab in combination with axitinib | Des.TrialAppr. |
| small cell lung carcinoma | Toripalimab | Des.TrialAppr. |
| soft tissue sarcoma | Toripalimab | Des.TrialAppr. |
0% of portfolio targets high unmet need diseases
23
overlap in 2+ diseases
0/5
candidate diseases
0
avg importance: 0
0
affecting portfolio
0% of portfolio targets high unmet need diseases
23
overlap in 2+ diseases
0/5
candidate diseases
0
avg importance: 0
0
affecting portfolio