4
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute myeloid leukemia | tigecycline | Orphan Designation | - |
| hyperphosphatasia with intellectual disability syndrome 6 | Heparin-binding epidermal growth factor-like growth factor | Orphan Designation | - |
| indolent plasma cell myeloma | Recombinant fusion protein consisting of the CD47-binding domain of human signal regulatory protein alpha (SIRPa) linked to the IgG4 Fc region of human IgG | Orphan Designation | - |
| necrotizing enterocolitis | Heparin-binding epidermal growth factor-like growth factor | Orphan Designation | - |
| osteosclerotic plasma cell myeloma | Recombinant fusion protein consisting of the CD47-binding domain of human signal regulatory protein alpha (SIRPa) linked to the IgG4 Fc region of human IgG | Orphan Designation | - |
| perinatal necrotizing enterocolitis | Heparin-binding epidermal growth factor-like growth factor | Orphan Designation | - |
| plasma cell myeloma | Recombinant fusion protein consisting of the CD47-binding domain of human signal regulatory protein alpha (SIRPa) linked to the IgG4 Fc region of human IgG | Orphan Designation | - |
| primary cutaneous T-cell non-Hodgkin lymphoma | 1-118-signal regulatory protein alpha (human) fusion protein with immunoglobulin G1 (human Fc fragment), dimer | Orphan Designation | - |