3
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| myoclonus, familial | Piracetam | Orphan Designation | - |
| myoclonus-cerebellar ataxia-deafness syndrome | Piracetam | Orphan Designation | - |
| myoclonus-dystonia syndrome | Piracetam | Orphan Designation | - |
| newborn respiratory distress syndrome | Protirelin | Orphan Designation | - |