2
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Fanconi anemia | Marinol | Orphan Designation | - |
| GM1 gangliosidosis | Marinol | Orphan Designation | - |
| Huntington disease | TestosteroneMarinol | Orphan Designation | - |
| Peters plus syndrome | Marinol | Orphan Designation | - |
| anorexia nervosa | Marinol | Orphan Designation | - |
| fatal familial insomnia | Testosterone | Orphan Designation | - |
| microphthalmia, syndromic 2 | Marinol | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 8a | Testosterone | Orphan Designation | - |