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University Hospitals Cleveland Medical Center — Rare Disease Pipeline | Kisho

University Hospitals Cleveland Medical Center

Other

1

Orphan Designations

0 approved, 1 designated

0

FDA Approvals

2

Active Trials

200 recruiting

3

Rare Diseases

across 4 areas

0

News (30d)

Quiet

University Hospitals Cleveland Medical Center is a company with 1 orphan drug designation across 3 rare diseases. Active clinical trials in 2 indications. gene therapy candidates in 1 disease. 21 active policy bills affect their portfolio.

Gene Therapy Active

Competitive Landscape

Diversified Portfolio

Disease-by-disease pipeline progression from orphan designation through clinical trials to FDA approval.

Source: FDA Orphan Drug Designations, ClinicalTrials.gov, Drugs@FDA

Approved: 0

In Trials: 2

Designated Only: 1

3 total diseases

Disease	Drug(s)	Stage
epilepsy	-	Des.TrialAppr.
osteosarcoma	a highly purified unmodified carbohydrate polymer which consists of (1,3) and (1,4)-beta-glycosidic linkages	Des.TrialAppr.
sickle cell disease	-	Des.TrialAppr.