2
Orphan Designations
1
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Kabuki syndrome 1 | nitric oxide | Orphan Designation | - |
| autosomal recessive osteopetrosis 3 | nitric oxide | Orphan Designation | - |
| idiopathic pulmonary fibrosis | nitric oxide | Orphan Designation | - |
| persistent fetal circulation syndrome | nitric oxide | Orphan Designation | - |
| primary ciliary dyskinesia 20 | nitric oxide | Orphan Designation | - |
| pulmonary hypertension, neonatal | nitric oxide | Orphan Designation | - |