2
Orphan Designations
1
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| post 5-alpha-reductase inhibitors treatment syndrome | Carmustine | Orphan Designation | - |
| post-treatment Lyme disease syndrome | Carmustine | Orphan Designation | - |
| pulmonary arterial hypertension | tacrolimus | Orphan Designation | - |
| treatment-refractory schizophrenia | Carmustine | Orphan Designation | - |