1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| glycogen storage disease IX | amylopectin | Orphan Designation | - |
| glycogen storage disease IXc | amylopectin | Orphan Designation | - |
| glycogen storage disease Ib | amylopectin | Orphan Designation | - |