1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Wolf-Hirschhorn syndrome | Potassium citrate and citric acid | Orphan Designation | - |
| double nail for fifth toe | Potassium citrate and citric acid | Orphan Designation | - |
| hemoglobin--variants for which the chain carrying the mutation 1S unknown or uncertain | Potassium citrate and citric acid | Orphan Designation | - |