16
Orphan Designations
0
FDA Approvals
23
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Aicardi-Goutieres syndrome 7 | Melatonin | Orphan Designation | - |
| Fabry disease | Melatonin | Orphan Designation | - |
| Smith-Lemli-Opitz syndrome | melatonin | Orphan Designation | - |
| Smith-Magenis syndrome | melatonin | Orphan Designation | - |
| Smith-McCort dysplasia 1 | melatonin | Orphan Designation | - |
| acute disseminated encephalomyelitis | melatonin | Orphan Designation | - |
| acute flaccid myelitis | melatonin | Orphan Designation | - |
| acute lymphoblastic leukemia | melatonin | Orphan Designation | - |
| acute radiation syndrome | melatonin | Orphan Designation | - |
| epidermolysis bullosa | Diacerein | Orphan Designation | - |
| exercise-induced malignant hyperthermia | Melatonin | Orphan Designation | - |
| heparin-induced thrombocytopenia | Melatonin | Orphan Designation | - |
| hepatocellular carcinoma | melatonin | Orphan Designation | - |
| malignant pancreatic neoplasm | melatonin | Orphan Designation | - |
| necrotizing enterocolitis | melatonin | Orphan Designation | - |
| optic neuritis | Melatonin | Orphan Designation | - |
| perinatal asphyxia | melatonin | Orphan Designation | - |
| primary biliary cholangitis | Melatonin | Orphan Designation | - |
| primary cutaneous lymphoma | Melatonin | Orphan Designation | - |
| retinitis pigmentosa | Melatonin | Orphan Designation | - |
| retinopathy of prematurity | Melatonin | Orphan Designation | - |
| short bowel syndrome | melatonin | Orphan Designation | - |
| subarachnoid hemorrhage | melatonin | Orphan Designation | - |