2
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| LIPE-related familial partial lipodystrophy | Cordarone | Orphan Designation | - |
| Larsen-like osseous dysplasia-short stature syndrome | Cordarone | Orphan Designation | - |
| Proteus-like syndrome | Cordarone | Orphan Designation | - |
| gastrointestinal stromal tumor | Cordarone | Orphan Designation | - |
| juvenile idiopathic arthritis | methotrexate | Orphan Designation | - |
| lice infestation | Cordarone | Orphan Designation | - |